sickle cell disease

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Here Are 5 of 2023's Biggest
Medical Breakthroughs

Dec 29, 2023 4:45 PM CST

Here Are 5 of 2023's Biggest Medical Breakthroughs

Alzheimer's meds, an OTC birth control pill, RSV vaccines all make ABC's list

(Newser) - If looking back at 2023 brings forth visions of dumpster fires in your head, take heart: There were some pretty amazing accomplishments over the past 12 months, notably on the health and science front. ABC News compiles some of the year's biggest medical breakthroughs, including a "significant milestone"...

In a Breakthrough, FDA
Backs Gene Editing Therapy

Dec 8, 2023 2:14 PM CST

In a Breakthrough, FDA Backs Gene Editing Therapy

New sickle cell disease treatments still face obstacles, including cost

(Newser) - Two gene therapies for sickle cell disease received government approval on Friday, one of which could represent a major turning point in medical treatments. To combat the blood disorder, the Food and Drug Administration for the first time endorsed gene editing therapy for humans, the New York Times reports. The...

This Treatment Could Be a Big First for Genetic Diseases

It Feels 'Like Being Stabbed
All Over.' A New Cure Is Closer

Nov 1, 2023 12:25 PM CDT

It Feels 'Like Being Stabbed All Over.' A New Cure Is Closer

Panel clears CRISPR gene-editing product for sickle cell disease patients; FDA to weigh in

(Newser) - Sickle cell disease is a painful, debilitating, and possibly deadly inherited disorder that currently can only be remedied with a bone marrow transplant. Now, Boston's Vertex Pharmaceuticals hopes exa-cel, its treatment developed with CRISPR Therapeutics, will soon be approved by the FDA following a thumbs-up from a panel of...

3 Stories